More Oligonucleotide Drugs Approved

Oligonucleotide drugs, also known as antisense drugs, are a type of medication designed to target specific genes in order to treat or prevent diseases. They work by binding to messenger RNA (mRNA) molecules and blocking their ability to produce certain Continue reading More Oligonucleotide Drugs Approved

Nusinersen API

Nusinersen is an oligonucleotide drug approved by the FDA in 2016 for the treatment of spinal muscular atrophy (SMA). SMA is a rare genetic disease that affects the muscles used for movement, breathing, and swallowing. Nusinersen is the first and Continue reading Nusinersen API